Spinal muscular atrophy: What is it?

If you were asked which genetic disease is the number one cause of death among babies in the United States, chances are spinal muscular atrophy would

San Clemente-based Hope for SMA, which works to fight spinal muscular atrophy, will present a dinner-and-entertainment fundraiser Friday night at Franciscan Gardens in San Juan Capistrano. 50% off! $25 for $50 in GolfHub Bucks towards Green Fees By

This award will support preclinical development of a CNS-delivered Gene Therapy for Spinal Muscular Atrophy. With funding from FSMA, Dr. Kaspar's team will initiate the studies needed for an Investigational New Drug (IND) application for this therapy

This award will support preclinical development of a CNS-delivered Gene Therapy for Spinal Muscular Atrophy. With funding from FSMA, Dr. Kaspar's team will initiate the studies needed for an Investigational New Drug (IND) application for this therapy